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  • Join the MDA Lock-Up Jailbird Fall Fundraising Challenge September 26, 2016
    MDA Lock-Up Jailbirds can earn their chance to win a pair of roundtrip airline tickets, Beats wireless headphones or an iPad Air 2. For every $100 Jailbirds raise between now and Friday, November 18  they will be automatically entered into the drawing.* Jailbirds are encouraged to track their progress at their Participant Center, and check […]
  • Catalyst Pharmaceuticals’ MG Drug Gets FDA Orphan Drug Designation September 21, 2016
    The investigational drug amifampridine phosphate (brand name Firdapse), under development by Catalyst Pharmaceuticals, has received U.S. Food and Drug Administration (FDA) Orphan Drug designation for the treatment of myasthenia gravis (MG). Amifampridine phosphate is a potassium channel inhibitor designed to prolong signals released from nerves and allow greater stimulation of muscles. The drug currently is […]
  • NIH Seeks Children and Caregivers to Participate in Quality of Life Study September 21, 2016
    Researchers at the National Institutes of Health (NIH) seek children with neuromuscular disorders (NMDs) and/or their caregivers (parent or legal guardian) to complete questionnaires. Researchers would like to develop a tool to better assess the quality of life of people with NMDs, such as muscular dystrophy. The goal of this study is to validate two different […]
  • Eteplirsen Granted Approval for DMD: Turning Promise into Progress September 19, 2016
    Today we couldn’t be happier as, together with the Duchenne community, we celebrate FDA accelerated approval of eteplirsen to treat kids and adults with some forms of Duchenne muscular dystrophy (DMD). “This is something that we’ve watched, and hoped and prayed for, and seen it develop over the last seven years or so,” said Josh […]
  • Meet the MDA Resource Specialist: Hugo September 16, 2016
    Since the tender ago of five, Hugo Trevino, who has Spinal Muscular Atrophy (SMA), has been involved with MDA. From participating in MDA Summer Camp as a child to rallying behind causes like Fill the Boot and Muscle Walk, Hugo has always been dedicated to helping others live longer and grow stronger. Now, as a […]

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